Image

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

Observing Elfabrio® safety and effectiveness in Fabry patients globally.

Recruiting
18 years and older
All
Phase N/A
**Study Overview**: This study is looking at how safe and effective a medicine called **Elfabrio®** is for people with **Fabry disease**, a rare genetic condition that affects how your body handles fat. The study is observational, which means doctors will watch and record details about patients who are already taking Elfabrio® as part of their regular care. **Who Can Join**: To be part of the study, you need to be over 18, have a confirmed diagnosis of Fabry disease, and either be taking or planning to take Elfabrio®. You also need to agree to be part of the study and complete some surveys. Some specific heart tests, like a **cardiac magnetic resonance imaging (cMRI)**, are also part of the study. **Key Points**: - **Length**: This is an ongoing study, and participants will be involved for an unspecified period as part of their regular treatment. - **Visits**: Regular medical visits are needed, where doctors will monitor your health and record data. - **Compensation**: There's no mention of payment, but participation may help improve future treatment for Fabry disease. Please consider if you meet these conditions and are comfortable with the study's requirements before deciding to participate.
Study details
    Fabry Disease

NCT06663358

Chiesi Farmaceutici S.p.A.

5 September 2026

Step 1 Get in touch with the nearest study center
We have submitted the contact information you provided to the research team at {{SITE_NAME}}. A copy of the message has been sent to your email for your records.
Would you like to be notified about other trials? Sign up for Patient Notification Services.
Sign up

Send a message

Enter your contact details to connect with study team


Email

View email

Phone

Phone country flag

View phone
Investigator Avatar

Primary Contact

  Other languages supported:

First name*
Last name*
Email*
Phone number*
Race*
Are you a healthy volunteer
Ethnicity*
Are you a healthy volunteer
Other language

FAQs

Learn more about clinical trials

What is a clinical trial?

A clinical trial is a study designed to test specific interventions or treatments' effectiveness and safety, paving the way for new, innovative healthcare solutions.

Why should I take part in a clinical trial?

Participating in a clinical trial provides early access to potentially effective treatments and directly contributes to the healthcare advancements that benefit us all.

How long does a clinical trial take place?

The duration of clinical trials varies. Some trials last weeks, some years, depending on the phase and intention of the trial.

Do I get compensated for taking part in clinical trials?

Compensation varies per trial. Some offer payment or reimbursement for time and travel, while others may not.

How safe are clinical trials?

Clinical trials follow strict ethical guidelines and protocols to safeguard participants' health. They are closely monitored and safety reviewed regularly.
Add a private note
  • abc Select a piece of text.
  • Add notes visible only to you.
  • Send it to people through a passcode protected link.